9 – GOSH

Great Ormond Street Hospital (United Kingdom) – www.gosh.nhs.uk

SCIDNET Principal Investigator: Emma Pendleton (Emma.Pendleton@gosh.nhs.uk)

GOSH’s mission is to provide world-class clinical care and training, pioneering new research and treatments, in partnership with others, for the benefit of children in the UK and worldwide. Across our departments and divisions we have a shared vision to produce world leading translational and patient-orientated research. We are always aspiring to develop new research and treatments across the breadth of paediatric specialities. Great Ormond Street Hospital for Children is fully committed to conducting high quality research in collaboration with our various academic and industry partners. GOSH is one of two centres in the UK designated to look after patients with SCID. As the larger of the two centres, GOSH sees more children with SCID than any other hospital in the UK. GOSH is also a major international referral centre for primary immunodeficiency and has a very strong bone marrow transplant programme for SCID. Through its collaboration with UCL GOSH has treated more children by gene therapy for primary immunodeficiency than any other centre worldwide.